Recent Posts
- Lupus Research Alliance Announces Expanded FDA Partnership to Enhance Lupus Treatment Development
- Poseida Therapeutics Hosts Gene Therapy R&D Day Highlighting New Scientific Advancements and Pipeline Focus
- Africa CDC blasts Moderna after it halts plans to build vaccine plant in Kenya
- Voyager Therapeutics Advances Gene Therapy Candidate in Partnership with Neurocrine Biosciences
- CureVac, MD Anderson Enter Strategic Cancer Vax Pact
AAV One-stop Solution
Tags
AAV2
AAV5
AAV based gene therapy
AAV Capsid
ALS
Alzheimer’s Disease
brain vasculature
cancer
CAR-T
Cell Therapy
chylomicronemia syndrome
COVID-19
COVID vaccine
CRISPR
CRISPR/Cas
Drug Development
dystrophin
eye disease
FDA
gene editing
gene therapy
genetic engineering
genome editing
GMP plasmid
hearing
heart disease
hemophilia
hepatitis research
HIV
immunotherapy
liver cancer
mRAN
mRNA
Neurodegenerative Diseases
Orphan Drug
Parkinson
rare disease
Retinoschisis
RNA
RNAi therapeutics
RNA vaccines
SARS-CoV-2
SMA Treatment
thyroid
zolgensma