dystrophin | PackGene Biotech

Gene editing system restores dystrophin function in stem cells from patients with Duchenne muscular dystrophy

Sep 1, 2023

This photo shows green dystrophin protein restored by dual-Cas3 in skeletal muscle derived from DMD patient iPSCs. Credit: Akitsu Hotta Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. On August 24...

Gene editing system restores dystrophin function in stem cells from patients with Duchenne muscular dystrophy

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AAV One-stop Solution

Gene editing system restores dystrophin function in stem cells from patients with Duchenne muscular dystrophy

Recent Posts

AAV One-stop Solution

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