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Opus Genetics Accelerates AAV Gene Therapy for Leber Congenital Amaurosis Following Key FDA RMAT Feedback
Nov 07 2025 -
Neurogene Doses First Participant in Registrational Embolden Trial of AAV Gene Therapy NGN-401 for Rett Syndrome
Nov 06 2025 -
UK Grants Innovation Passport to Solid Biosciences’ AAV Gene Therapy SGT-003 for Duchenne Muscular Dystrophy
Nov 06 2025 -
MavriX Bio Doses First Patient in Landmark AAV Gene Therapy Trial for Angelman Syndrome
Nov 06 2025 -
India Achieves Major Healthcare Milestone with World’s First Humanized CAR-T Therapy
Nov 05 2025 -
CHLA Enhances Gene Therapy Safety: Elevidys Protocol Revised for High-Risk Duchenne Patients
Nov 05 2025 -
Sarepta DMD Candidates Fail to Hit Primary Endpoint in Phase III Confirmatory Trial
Nov 04 2025 -
Azalea Therapeutics Launches with $82M Funding to Pioneer In Vivo Cell Engineering
Nov 04 2025 -
Genprex Secures Key European Patent for Gene Therapy in Combination with PD-1 Inhibitors
Nov 04 2025