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Regenxbio Reports Positive Functional Outcomes for RGX-202 AAV Gene Therapy in Duchenne
Jun 05 2025 -
Ocugen Announces Key Licensing Agreement for OCU400 in South Korea: A Novel AAV Gene Therapy for RP
Jun 05 2025 -
HHS Secretary and Top Health Officials Pledge Support for Cell and Gene Therapies at FDA Roundtable
Jun 05 2025 -
Sarepta Therapeutics Receives FDA Platform Technology Designation for its rAAVrh74 Viral Vector
Jun 04 2025 -
Gilead Prepares Outpatient BCMA CAR T Entry to Challenge J&J Multiple Myeloma Market
Jun 04 2025 -
Elpis Biopharmaceuticals Collaborates with Singapore General Hospital to Advance Next-Generation CAR-T Therapies for Blood Cancers
Jun 04 2025 -
Beam Therapeutics’ BEAM-101 Receives FDA Orphan Drug Designation for Sickle Cell Disease
Jun 03 2025 -
New CBER Director Pledges Swift Action, Flexibility for Rare Disease Treatments
Jun 03 2025 -
uniQure Nears BLA Submission for AAV-Based Gene Therapy AMT-130 for Huntington’s Disease
Jun 02 2025