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RiboX Receives FDA IND Clearance for circRNA-Based In Vivo CAR-T Therapy RXIM002
Aug 09 2026 -
Aspen Neuroscience Receives FDA RMAT Designation for Autologous iPSC-Derived Cell Therapy in Parkinson’s Disease
Aug 07 2026 -
Precision BioSciences Reports Clinical Evidence of cccDNA Elimination with Gene Editing Therapy for Chronic Hepatitis B
Aug 06 2026 -
Pacira Reports Two-Year Phase 1 Data for HCAd Gene Therapy PCRX-201 in Knee Osteoarthritis
Aug 06 2026 -
Sarepta Reports Q2 2026 Results as Precision Genetic Medicine Pipeline Advances Toward Key Clinical Readouts
Aug 05 2026 -
Tenaya Reports Clinical Progress for AAV Gene Therapies TN-201 and TN-401 in Inherited Cardiomyopathies
Aug 05 2026 -
Galibra Receives FDA Orphan Drug and Rare Pediatric Disease Designations for AAV Gene Therapy in SSADH Deficiency
Aug 05 2026 -
Kriya Reports Preclinical Data Showing AAV-FGF21 Gene Therapy Extended Health Span and Lifespan in Aged Mice
Aug 05 2026 -
Eli Lilly Discontinues AAV-Based GBA1 Gene Therapy Trial in Gaucher Disease Type 1
Aug 05 2026