Industry News
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FDA Approves First LVV-based Gene Therapy for Wiskott-Aldrich Syndrome
Dec 10 2025 -
FDA Set to Require Randomized Trials and Superiority Data for Full CAR T Approval
Dec 09 2025 -
Japan Grants Pioneering AAV Gene Therapy Designations to AskBio for Parkinson’s and Heart Failure Programs
Dec 09 2025 -
Kelonia’s In Vivo CAR-T Therapy KLN-1010 Achieves 100% MRD-Negative Responses in Early Multiple Myeloma Data
Dec 09 2025 -
Gene Therapy Upstart EpilepsyGTx Secures $33 Million Series A to Advance AAV-Based Epilepsy Program
Dec 09 2025 -
Gene-Edited BE-CAR7 Cells Achieve Deep Remission in Aggressive T-Cell Leukemia
Dec 08 2025 -
New Phase 3 Data for AAV Gene Therapy OAV101 IT Shows Motor Improvement in Older Children and Teens with SMA
Dec 08 2025 -
CSL Behring Reports Durable Five-Year Efficacy for AAV Gene Therapy Hemgenix in Hemophilia B
Dec 07 2025 -
Beam Therapeutics’ Base Editing Gene Therapy Resolves Anemia in SCD Patients
Dec 06 2025