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Gene-Edited BE-CAR7 Cells Achieve Deep Remission in Aggressive T-Cell Leukemia
Dec 08 2025 -
New Phase 3 Data for AAV Gene Therapy OAV101 IT Shows Motor Improvement in Older Children and Teens with SMA
Dec 08 2025 -
CSL Behring Reports Durable Five-Year Efficacy for AAV Gene Therapy Hemgenix in Hemophilia B
Dec 07 2025 -
Beam Therapeutics’ Base Editing Gene Therapy Resolves Anemia in SCD Patients
Dec 06 2025 -
Vertex Presents Transformative Gene Therapy Data in Children with Sickle Cell Disease and Thalassemia
Dec 06 2025 -
Encoded Therapeutics’ AAV Gene Therapy ETX101 Shows 78% Seizure Reduction in Dravet Syndrome Trial
Dec 05 2025 -
NCH’s AAV Gene Therapy Shows Early Promise in Neurodevelopment Disorders
Dec 05 2025 -
Dual-Action AAV Gene Therapy Restores Cardiac Function in Heart Failure Mouse Model
Dec 04 2025 -
AAV Gene Therapy AMT-130 Faces Regulatory Hurdle
Dec 04 2025