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Beam Therapeutics’ Base Editing Gene Therapy Resolves Anemia in SCD Patients
Dec 06 2025 -
Encoded Therapeutics’ AAV Gene Therapy ETX101 Shows 78% Seizure Reduction in Dravet Syndrome Trial
Dec 05 2025 -
NCH’s AAV Gene Therapy Shows Early Promise in Neurodevelopment Disorders
Dec 05 2025 -
Dual-Action AAV Gene Therapy Restores Cardiac Function in Heart Failure Mouse Model
Dec 04 2025 -
AAV Gene Therapy AMT-130 Faces Regulatory Hurdle
Dec 04 2025 -
Capricor Therapeutics Reports Positive Phase 3 Results for Cell Therapy in DMD
Dec 03 2025 -
Triple-Drug Strategy May Unlock Repeat Dosing and Expand Eligibility for DMD AAV Gene Therapy
Dec 03 2025 -
Roatán Island Pushes Regulatory Boundaries for Anti-Aging Gene Therapies
Dec 02 2025 -
Latus Bio AAV Gene Therapy LTS-101 Cleared by FDA to Treat Fatal CLN2 Disease
Dec 02 2025