-
AviadoBio’s ASPIRE-FTD AAV Gene Therapy Trial Opens in the UK for Frontotemporal Dementia
May 16 2025 -
Rocket Pharma’s AAV Gene Therapy Shows Promise in Inherited Heart Disease
May 16 2025 -
Infant with Rare Genetic Disorder Successfully Treated with Customized mRNA-based CRISPR Gene Editing Therapy at CHOP and Penn Medicine
May 15 2025 -
PolTREG Cell Therapy Receives Positive EMA Opinion for Pediatric Type 1 Diabetes Therapy
May 15 2025 -
BrainChild Bio’s CAR T-cell Therapy for DIPG Receives RMAT Designation
May 15 2025 -
Genespire Presents Positive Preclinical Dosing Data for In Vivo Gene Therapy for Methylmalonic Acidemia
May 14 2025 -
Latus Bio Announces Novel AAV Capsid AAV-Ep+ Demonstrates Robust Brain Transduction and Therapeutic Protein Expression in Preclinical Studies
May 14 2025 -
Rgenta’s RSwitch Platform Reported to Regulate Gene Therapy Transgene Expression
May 13 2025 -
REGENXBIO Announces FDA Acceptance and Priority Review of BLA for RGX-121 Gene Therapy in Hunter Syndrome
May 13 2025