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Kyowa Kirin and Orchard Therapeutics’ Gene Therapy for MLD Earns Key Designations in Japan and Saudi Arabia
Oct 28 2025 -
Safety Concern Halts Intellia’s Phase III CRISPR Gene Therapy Trials
Oct 27 2025 -
Medera Advances Cardiac AAV Gene Therapy to Phase 2 for Heart Failure
Oct 27 2025 -
BMS CAR T-Cell Therapy Shows Potential for ‘Immune Reset’ in Severe Autoimmune Diseases
Oct 27 2025 -
Eli Lilly Expands Genetic Medicine Portfolio with Acquisition of Adverum Biotechnologies
Oct 24 2025 -
Moderna Halts Development of CMV mRNA Vaccine After Phase 3 Failure
Oct 23 2025 -
International Experts Publish First Consensus Guidelines for Hearing Loss Gene Therapy Trials
Oct 23 2025 -
Genprex Gene Therapy Shows Strong Preclinical Efficacy in Lung Cancer
Oct 23 2025 -
Nanoscope’s AAV Gene Therapy Maintains Clinically Meaningful Vision Improvements in Retinitis Pigmentosa
Oct 22 2025