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CRISPR Therapeutics Highlights Promising In Vivo Gene Editing Data
May 07 2025 -
Neurocrine Returns Two Gene Therapy Programs to Voyager Amidst Ongoing CNS Collaboration
May 07 2025 -
Solve FSHD Invests $3 Million in Armatus Bio’s AAV-miRNA Therapy for Muscular Dystrophy
May 07 2025 -
Sangamo Therapeutics Achieves Key Milestones for Fabry Disease Gene Therapy, Paving Way for Potential BLA Submission
May 06 2025 -
Beacon Therapeutics Reports Positive Interim Phase 2 Data in X-Linked Retinitis Pigmentosa
May 06 2025 -
Nuevocor Secures $45 Million Series B Funding to Advance Novel Cardiomyopathy Therapies
May 06 2025 -
J&J’s Gene Therapy for Rare Eye Disease Fails Primary Endpoint in Phase 3 Trial
May 05 2025 -
FDA Grants RMAT Designation to 4DMT’s 4D-150 for Diabetic Macular Edema
May 05 2025 -
Opus Genetics’ OPGx-LCA5 Shows Sustained Vision Improvement at One Year in Phase 1/2 Study
May 05 2025