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AAV Gene Therapy in Ocular Diseases
Apr 18 2025 -
Breakthroughs in CAR-T Cell Therapy for Colorectal Cancer
Apr 11 2025 -
Dual-AAV Gene Therapy Corrects Dravet Syndrome in Mice
Apr 07 2025 -
π-Icosa Derived AAV Capsid PG007 Enhanced Micro-Dystrophin Delivery in DMD Model
Mar 28 2025 -
Engineered AAV Capsids: Muscle-Specific Transduction and Liver Detargeting
Mar 21 2025 -
Advancing Bleeding Disorder Treatments: AAV-Based Gene Therapy Breakthroughs
Mar 13 2025 -
Case Study: Developing Target Product Profiles (TPPs) for AAV-Based Therapies
Mar 06 2025 -
Breaking Barriers: PackGene Facilitates Gene Therapies for OTOF Hearing Loss and SPG56
Feb 27 2025 -
CRISPR, Base Editors, and Prime Editors in Gene Therapy
Feb 17 2025