Industry News
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Apertura and RSRT Join Forces to Advance Brain-Targeting Gene Therapy for Rett Syndrome Using Novel AAV Capsid
Apr 30 2025 -
FDA Approves Abeona Therapeutics’ First and Only Gene Therapy for RDEB Wounds
Apr 29 2025 -
Genprex Licenses Exclusive Patent for Quaratusugene Ozeplasmid Gene Therapy in Mesothelioma
Apr 28 2025 -
Ray Therapeutics Receives $8M CIRM Grant to Advance RTx-015 Gene Therapy for Retinitis Pigmentosa
Apr 28 2025 -
YolTech Therapeutics Announces Promising Interim Data for Novel In Vivo Base Editing Therapy YOLT-101 in Heterozygous Familial Hypercholesterolemia (HeFH)
Apr 28 2025 -
Senti Bio Reports Positive Preliminary Phase 1 Data for Logic Gated CAR-NK Therapy SENTI-202 in Relapsed/Refractory AML
Apr 28 2025 -
BlackfinBio Receives FDA Clearance to Initiate Phase 1/2 Clinical Trial of Novel Gene Therapy BFB-101 for Rare Neurological Disorder SPG47
Apr 28 2025 -
Innorna’s IN013 Receives FDA Rare Pediatric Disease and Orphan Drug Designations for Wilson Disease
Apr 27 2025 -
European Commission Grants Orphan Drug Designation to Dyne Therapeutics’ DYNE-251 for Duchenne Muscular Dystrophy
Apr 25 2025