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Adenine Base Editing Restores Hearing in a Humanized Mouse Model
Aug 22 2025 -
From Discovery to Clinical Impact: The Evolution of AAV Vector Engineering in Gene Therapy, Cell Therapy, and Regenerative Medicine
Aug 08 2025 -
AAV amiRNAs with Engineered Scaffolds for Potent Gene Silencing In Vivo
Jul 11 2025 -
PackGene’s π-Icosa Platform Delivers Next-Generation AAV Capsid PG007 for Muscle-Specific Gene Therapy
Jun 27 2025 -
AAV Gene Therapy in Cardiovascular Disease
Jun 15 2025 -
AAV Vector Characterization: Analytical Methods for Full, Empty and Partial Capsid Ratio Assessment
May 30 2025 -
ASGCT 2025: Insights from Featured Talks and Posters
May 16 2025 -
AAV Gene Therapy in Cancer: Insights from the AACR Annual Meeting 2025
May 02 2025 -
AAV Gene Therapy in Ocular Diseases
Apr 18 2025