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AAV Gene Therapy Shows Promise for Treating LRAT-Associated Retinitis Pigmentosa
Mar 10 2026 -
Solid Biosciences Secures $240 Million Private Placement to Support Gene Therapy Pipeline
Mar 10 2026 -
Benitec Reports Encouraging Early Clinical Results for AAV9 Gene Therapy BB-301 in OPMD
Mar 09 2026 -
Precision BioSciences’ AAV Gene Editing Therapy PBGENE-DMD Receives FDA Fast Track Designation
Mar 09 2026 -
Sangamo Advances AAV Gene Therapy ST-920 Toward FDA Accelerated Approval for Fabry Disease
Mar 09 2026 -
Atamyo Therapeutics Shows Promising Early Clinical Data for AAV Gene Therapy ATA-200 in LGMD-R5 Muscular Dystrophy
Mar 09 2026 -
AAV-Mediated Parkin Gene Therapy Shows Promising Rescue of Dopaminergic Neurons in Parkinson’s Disease Models
Mar 05 2026 -
Passage Bio Advances AAV Gene Therapy Program for Frontotemporal Dementia and Expands Neurodegenerative Pipeline
Mar 04 2026 -
FDA Details Reasons for Rejecting Regenxbio’s AAV Gene Therapy RGX-121 for Hunter Syndrome
Mar 04 2026