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Characteristic changes in astrocyte properties during astrocyte-to-neuron conversion induced by NeuroD1/Ascl1/Dlx2
Author:
Qing He, Zhen Wang, Yuchen Wang, Mengjie Zhu, Zhile Liang, Kanghong Zhang, Yuge Xu, Gong Chen
Journal: Neural Regeneration Research
Doi: https://www.doi.org/10.4103/NRR.NRR-D-23-01897
Jun 2025 -
Deciphering signaling mechanisms and developmental dynamics in extraembryonic mesoderm specification from hESCs
Author:
Baohua Niu, Da Wang, Yingjie Hu, Yundi Wang, Gaohui Shi, Zhongying Chen, Lifeng Xiang, Chi Zhang, Xuesong Wei, Ruize Kong, Hongzhi Cai, Weizhi Ji, Yu Yin, Tianqing Li & Zongyong Ai
Journal: Cell lineage, Pluripotency, Pluripotent stem cells
Doi: https://www.doi.org/10.1038/s41467-025-59491-x
May 21 2025 -
The paraventricular thalamus mediates visceral pain and anxiety-like behaviors via two distinct pathways
Author:
Di Li, Yong-Chang Li, Zheng-Yan Zhu, Fu-Chao Zhang, Qiu-Ying Zhao, Jia-Hui Jiang, Biyu Shen, Yong Tang, Guang-Yin Xu
Journal: Neuron
Doi: https://www.doi.org/10.1016/j.neuron.2025.04.019
May 8 2025 -
Cross-species tropism of AAV. CPP. 16 in the respiratory tract and its gene therapies against pulmonary fibrosis and viral infection
Author:
Zhi Yang, Yizheng Yao, Xi Chen, Victoria Madigan, Shanrui Pu, Xianqun Fan, Jun Pu, Fengfeng Bei
Journal: Cell Reports Medicine
Doi: https://www.doi.org/10.1016/j.xcrm.2025.102144
May 22 2025 -
Viral-mediated knockdown of Atxn2 attenuates TDP-43 pathology and muscle dysfunction in the PFN1C71G ALS mouse model
Author:
Zachary C. E. Hawley, Xueying Li, Dora Bodnar, Yuanzheng Gu, Yi Luo, Daniel Ferretti, Adam Sheehy, Rachelle Driscoll, Maria I. Zavodszky, Shaolong Cao, Isabel Isaza, Luke Jandreski, Yuqing Liu, Thomas Carlile, Shih-Ching Lo, Anna Grimard, Shawn Bourque, Aditya Utturkar, Samantha Desmarais, H. Moore Arnold, Dann Huh, Edward Guilmette & Deborah Y. Kwon
Journal: Acta Neuropathologica Communications
Doi: https://www.doi.org/10.1186/s40478-025-02005-z
May 24 2025 -
Transcription Factor‐Based Gene Therapy Enables Functional Repair of Rat Following Chronic Ischemic Stroke
Author:
Tao Wang, Xu Wang, Shanggong Liu, Menglei Li, Kaiying Wan, Jiajun Zheng, Kai Liao, Jinyu Wang, Kaiming Zou, Lu Wang, Hao Xu, Wenliang Lei, Gong Chen, Wen Li
Journal: CNS Neuroscience & Therapeutics
Doi: https://www.doi.org/10.1111/cns.70448
May 22 2025 -
PEBL, a component-based Chinese medicine, reduces virus-induced acute lung injury by targeting FXR to decrease ACE2 levels
Author:
Liling Yang, Xiangjun Zhou, Junshan Liu, Guangli Yang, Weifu Tan, Hongyan Ding, Xiaochuan Fang, Jingtao Yu, Wei Li, Jiayang He, Huihui Cao, Qinhai Ma, Linzhong Yu, Zibin Lu
Journal: Journal of Advanced Research
Doi: https://www.doi.org/10.1016/j.jare.2025.05.003
May 3 2025 -
Preclinical studies of an AAV8-CYP4V2 gene therapy VGR-R01 for the treatment of Bietti crystalline dystrophy
Author:
Wenjing Luo, Lu Guo, Liang Lu, Nan Huang, Yezheng Tao, Yufei Zhang, Yanrong Cao, Shin-Shay Tian, Xiaoping Zhao, Xi Zhu
Journal: Molecular Therapy
Doi: https://www.doi.org/10.1016/j.omtm.2025.101460 External Link
Apr 3 2025 -
Neural organoids protect engineered heart tissues from glucolipotoxicity by transferring versican in a co-culture system
Author:
Baochen Bai, Jiting Li, Ze Wang, Yuhan Yang, Jieqing He, Gonglie Chen, Yufan Zhang, Yan Qi, Zhongjun Wan, Lin Cai, Run Wang, Kai Wang, Dongyu Zhao, Jingzhong Zhang, Weihua Huang, Ronald X Xu, Mingzhai Sun, Xiao Han, Yan Liu, Donghui Zhang, Wanying Zhu, Jian Liu, Yuxuan Guo
Journal: BioRxiv
Doi: https://www.doi.org/10.1101/2025.05.07.652597
May 12 2025 -
An engineered intravitreal injection RPE-tropic AAV vector expressing a bispecific antibody binding VEGF-A and ANG-2 rescues nAMD in animal models and …
Author:
Yuan Cai, Yonghao Gu, Jie Zhang, Ying Zhu, Zhen Ma, Qin He,Yongjia Sun, Mengmeng Yuan, Xiaojun Li, Kai Zhu, Bolong Miao, Jin Zhao, Juan Liu, Min Tang, Dali Tong, Lixia Feng, Ming Ma, Guisheng Zhong, Zilong Qiu, Tian Xue
Journal: Research
Doi: https://www.doi.org/10.34133/research.0717
May 8 2025 -
Engineering novel AAV capsids by global de-targeting and subsequent muscle-specific tropism in mice and NHPs
Author:
Yue Pan, Yujian Zhong, Huan Chen, Youwei Zhang, Zhiyong Dai, Junlin Chen, Keqin Tan, Xiaoqu Chen, Danlan Qiu, Longxiang Sheng, Xinping Tan, Ying Fan, Ye Bu, Zexin Zhou, Zhiming Yang, Rui Duan, Min Guan, Guangping Gao, Huapeng Li
Journal: BioRxiv
Doi: https://www.doi.org/10.1101/2025.05.19.654800
May 19 2025 -
Diminished MYCN Dosage Endows Cavitary Transformation in Retinoblastoma
Author:
Mingpeng Xu, Hanhan Shi, Yongning Shen, Ludi Yang, Yu Luan, Xiang Gu, Xuyang Wen, Chuandi Zhou, Renbing Jia, Xunda Ji, Peiquan Zhao, Minglei Han, Jiayan Fan, Peiwei Chai
Journal: Ophthalmology Science
Doi: https://www.doi.org/10.1016/j.xops.2025.100820
May 6 2025