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Krystal Biotech Receives FDA Platform Designation for Gene Therapy Vector
Oct 16 2025 -
Groundbreaking LVV Gene Therapy Cures ‘Bubble Baby’ Disease in Pivotal Long-Term Study
Oct 15 2025 -
Liberate Bio Raises $31M for In Vivo CAR-M Therapy, Targeting Safer Immune Reset
Oct 15 2025 -
Regeneron’s AAV Gene Therapy Restores Hearing in Most Children with Profound Genetic Deafness
Oct 14 2025 -
Pioneering AAV Gene Therapy Reverses Early Kidney Damage in Diabetic Mice
Oct 14 2025 -
FDA Accepts Rocket Pharma’s Gene Therapy for Severe LAD-I
Oct 14 2025 -
Antibody-Clearing Enzyme Allows First AAV Gene Therapy Dosing in Previously Ineligible Patient
Oct 13 2025 -
Next-Generation AAV Gene and Epigenetic Therapies Promise Opioid-Free, Long-Term Pain Relief
Oct 13 2025 -
Abeona Therapeutics’ AAV Gene Therapy Selected for FDA Rare Disease Endpoint Advancement Pilot Program
Oct 13 2025