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Characteristic changes in astrocyte properties during astrocyte-to-neuron conversion induced by NeuroD1/Ascl1/Dlx2
Author:
Qing He, Zhen Wang, Yuchen Wang, Mengjie Zhu, Zhile Liang, Kanghong Zhang, Yuge Xu, Gong Chen
Journal: Neural Regeneration Research
Doi: https://www.doi.org/10.4103/NRR.NRR-D-23-01897
Jun 2025 -
Selective RNAi silencing of Schwann cell Piezo1 alleviates mechanical hypersensitization following peripheral nerve injury
Author:
Brandon Itson-Zoske, Uarda Gani, Alexander Mikesell, Chensheng Qiu, Fan Fan, Cheryl L Stucky, Quinn H Hogan, Seung Min Shin, Hongwei Yu
Journal: Mol Ther Methods Clin Dev
Feb 12 2025 -
Non-invasive detection of allele-specific CRISPR-SaCas9-KKH disruption of TOR1A DYT1 allele in a xenograft mouse model
Author:
Katia E Maalouf, Dawn Madison Frederick, Nutan Sharma, Edwina Abou Haidar, Tianhe Xiao, Justin Seungkyu Han, Mohammed S Mahamdeh, Roy J Soberman, David Rufino-Ramos, Benjamin P Kleinstiver, Hyder A Jinnah, Christine A Vaine, D Cristopher Bragg, Koen Breyne
Journal: Mol Ther Nucleic Acids
Jan 28 2025 -
Single-cut gene therapy in a one-step generated rhesus monkey model of Duchenne muscular dystrophy
Author:
Raoxian Bai, Ting Zhang, Jie Liu, Junyu Zhang, Jiao Yang, Siyu Liu, Shangang Li, Shu Zhang, Shiwen Wu, Yongchang Chen
Journal: Cell Reports Medicine
Mar 26 2025 -
Intratumoral gene delivery of 4-1BBL boosts IL-12-triggered anti-glioblastoma immunity
Author:
Taral R. Lunavat, Sanne M. van de Looij, Charles P. Couturier, Tyler E. Miller, Maryam Schübel, Emilio Di Ianni, Yi Sun, Thomas S. van Solinge, Emily Grandell, Vamsi Mangena, Russell W. Jenkins, Xandra O. Breakefield, Koen Breyne
Journal: bioRxiv
Feb 5 2025 -
Single Administration of AAV‐mAtp6v1b2 Gene Therapy Rescues Hearing and Vestibular Disorders Caused by Atp6v1b2‐Induced Lysosomal Dysfunction in Hair?…
Author:
Gege Wei, Xue Gao, Yijin Chen, Haifeng Feng, Guojie Dong, Weihao Zhao, Guangqin Wang, Pu Dai, Yongyi Yuan
Journal: Advanced Science
Mar 11 2025 -
Multilayered HIV-1 resistance in HSPCs through CCR5 Knockout and B cell secretion of HIV-inhibiting antibodies
Author:
William N. Feist, Kaya Ben-Efraim, Alvaro Amorin, Theodora U. J. Bruun, Hana Y. Ghanim, Theresa M. McLaughlin, Amanda M. Dudek & Matthew H. Porteus
Journal: Nature Communications
Apr 1 2025 -
Enhanced SIRT3 expression restores mitochondrial quality control mechanism to reverse osteogenic impairment in type 2 diabetes mellitus
Author:
Yansi Xian, Tao Shen, Rui Peng, Xueying An, Yu Ben, Qing Jiang & Baosheng Guo
Journal: Bone Research
Mar 3 2025 -
STING agonist-based ER-targeting molecules boost antigen cross-presentation
Author:
Xiafeng Wang, Lixiao Xing, Juan Jiang, Wei Yu, Hao Yang, Xinmin Liu, Yixin Chen, Jing Liu, Wei Xu, Zezhong Liu, Shibo Jiang, Lu Lu & Ji Wang
Journal: Nature
Mar 26 2025 -
Specific and efficient RNA A-to-I editing through cleavage of an ADAR inhibitor
Author:
Guangye Li, Guo-Hua Yuan, Qingyang Ni, Bei Yang, Li Yang & Jia Chen
Journal: Nature Biotechnology
Mar 26 2025 -
Identification of the core regulatory program driving NEUROD1-induced neuronal reprogramming
Author:
Wen Li, Xining Li, Qingpei Huang, Xiaopeng Luo, Xiaoying Fan
Journal: Cell Reports
Apr 1 2025 -
Brain‐Wide Neuroregenerative Gene Therapy Improves Cognition in a Mouse Model of Alzheimer’s Disease
Author:
Zheng Wu, Yu Xie, Shreya Swaminathan, Wenyu Ji, Yaowei Guo, Gong Chen
Journal: Advanced Science
Feb 14 2025