The initial focus of the CGT Access Model will be on Sickle Cell Disease (SCD), a genetic blood disorder that predominantly affects Black Americans, impacting over 100,000 people in the U.S. SCD patients often endure severe pain, leading to frequent hospitalizations, and have a life expectancy 20 years shorter than the national average.
AIR’s role will be crucial in monitoring the implementation and outcomes of the CGT Access Model. The organization will develop and execute a comprehensive data collection and analysis plan to assess both health outcomes and financial indicators. AIR’s efforts will also include disseminating findings at conferences to foster innovation in the field.
“The Cell and Gene Therapy Access Model has the potential to make groundbreaking treatments more widely available to those who need them and reduce long-term healthcare costs,” said Timothy Hill, AIR senior vice president, who leads the institution’s Health Division. “We look forward to working with CMS and our partners to test innovative solutions that can improve people’s lives and create a more equitable world.”
https://www.globenewswire.com/news-release/2024/08/21/2933709/0/en/American-Institutes-for-Research-To-Help-Implement-Federal-Program-Aimed-at-Increasing-Access-to-Transformative-Cell-and-Gene-Therapy-Treatments.html
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